Our Pipeline

Skyhawk is advancing a diverse pipeline of RNA-targeted small molecule therapies across neurology, oncology, and fibrotic disease.

Clinical & Preclinical Programs

Asset Target Indication Area Partner Development Stage
SKY-0515 HTT Huntington's Disease Neurology Skyhawk
Preclinical Phase 1 Phase 2 Phase 3
Phase 2/3
SKY-0925 Undisclosed Rare Neurological Disease Neurology Skyhawk
Preclinical Phase 1 Phase 2 Phase 3
Preclinical
SKY-4100 Undisclosed Rare Neurological Disease Neurology Skyhawk
Preclinical Phase 1 Phase 2 Phase 3
Preclinical
SKY-2100 Undisclosed Rare Neurological Disease Neurology Skyhawk
Preclinical Phase 1 Phase 2 Phase 3
Preclinical
Undisclosed Undisclosed Undisclosed Undisclosed Genentech
Preclinical Phase 1 Phase 2 Phase 3
Preclinical
Undisclosed Undisclosed Undisclosed Undisclosed Sanofi
Preclinical Phase 1 Phase 2 Phase 3
Preclinical
Undisclosed Undisclosed Undisclosed Undisclosed Merck KGaA
Preclinical Phase 1 Phase 2 Phase 3
Preclinical
Undisclosed Undisclosed Undisclosed Undisclosed Takeda
Preclinical Phase 1 Phase 2 Phase 3
Preclinical
Undisclosed Undisclosed Undisclosed Undisclosed Bristol Myers Squibb
Preclinical Phase 1 Phase 2 Phase 3
Preclinical
Undisclosed Undisclosed Undisclosed Undisclosed Merck
Preclinical Phase 1 Phase 2 Phase 3
Preclinical
Undisclosed Undisclosed Undisclosed Undisclosed Ipsen
Preclinical Phase 1 Phase 2 Phase 3
Preclinical